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Drugs target to HTT
Drug name | Drug type | Disease/phenotype | Mechanism of action(MoA) | Phase | Status | Source |
---|---|---|---|---|---|---|
TOMINERSEN | Oligonucleotide | Huntington disease | Huntingtin mRNA antisense inhibitor | 3.0 | Completed | ClinicalTrials |
TOMINERSEN | Oligonucleotide | Huntington disease | Huntingtin mRNA antisense inhibitor | 1.0 | Completed | ClinicalTrials |
TOMINERSEN | Oligonucleotide | Huntington disease | Huntingtin mRNA antisense inhibitor | 3.0 | Active, not recruiting | ClinicalTrials |
TOMINERSEN | Oligonucleotide | Huntington disease | Huntingtin mRNA antisense inhibitor | 2.0 | Completed | ClinicalTrials |