Drugs target to HTT

Drug name Drug type Disease/phenotype Mechanism of action(MoA) Phase Status Source
TOMINERSENOligonucleotideHuntington diseaseHuntingtin mRNA antisense inhibitor3.0CompletedClinicalTrials
TOMINERSENOligonucleotideHuntington diseaseHuntingtin mRNA antisense inhibitor1.0CompletedClinicalTrials
TOMINERSENOligonucleotideHuntington diseaseHuntingtin mRNA antisense inhibitor3.0Active, not recruitingClinicalTrials
TOMINERSENOligonucleotideHuntington diseaseHuntingtin mRNA antisense inhibitor2.0CompletedClinicalTrials