Drugs target to SMN1

Drug name Drug type Disease/phenotype Mechanism of action(MoA) Phase Status Source
ONASEMNOGENE ABEPARVOVECGenenoneSurvival motor neuron protein positive modulator3['Active, not recruiting', 'Active, not recruiting', 'Active, not recruiting', 'Active, not recruiting', 'Active, not recruiting', 'Active, not recruiting', 'Completed', 'Active, not recruiting', 'Active, not recruiting', 'Completed', 'Active, not recruiting', 'Active, not recruiting', 'Not yet recruiting']['ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials', 'ClinicalTrials']