Drugs target to NAE1

Drug name Drug type Disease/phenotype Mechanism of action(MoA) Phase Status Source
PEVONEDISTATSmall moleculeacute myeloid leukemiaNEDD8 activating enzyme inhibitor1.0RecruitingClinicalTrials
PEVONEDISTATSmall moleculeintrahepatic cholangiocarcinomaNEDD8 activating enzyme inhibitor2.0SuspendedClinicalTrials
PEVONEDISTATSmall moleculemyelodysplastic syndromeNEDD8 activating enzyme inhibitor1.0CompletedClinicalTrials
PEVONEDISTATSmall moleculemetastatic melanomaNEDD8 activating enzyme inhibitor1.0CompletedClinicalTrials
PEVONEDISTATSmall moleculetherapy related acute myeloid leukemia and myelodysplastic syndromeNEDD8 activating enzyme inhibitor1.0Active, not recruitingClinicalTrials
PEVONEDISTATSmall moleculeneoplasmNEDD8 activating enzyme inhibitor1.0TerminatedClinicalTrials
PEVONEDISTATSmall moleculeacute myeloid leukemiaNEDD8 activating enzyme inhibitor1.0Active, not recruitingClinicalTrials
PEVONEDISTATSmall moleculeacute myeloid leukemiaNEDD8 activating enzyme inhibitor3.0Active, not recruitingClinicalTrials
PEVONEDISTATSmall moleculeacute myeloid leukemiaNEDD8 activating enzyme inhibitor2.0CompletedClinicalTrials
PEVONEDISTATSmall moleculenon-small cell lung carcinomaNEDD8 activating enzyme inhibitor2.0Active, not recruitingClinicalTrials
PEVONEDISTATSmall moleculeacute myeloid leukemiaNEDD8 activating enzyme inhibitor2.0TerminatedClinicalTrials
PEVONEDISTATSmall moleculeacute myeloid leukemiaNEDD8 activating enzyme inhibitor2.0WithdrawnClinicalTrials
PEVONEDISTATSmall moleculechronic myelomonocytic leukemiaNEDD8 activating enzyme inhibitor2.0CompletedClinicalTrials
PEVONEDISTATSmall moleculeacute myeloid leukemiaNEDD8 activating enzyme inhibitor2.0Active, not recruitingClinicalTrials
PEVONEDISTATSmall moleculeneoplasmNEDD8 activating enzyme inhibitor1.0CompletedClinicalTrials
PEVONEDISTATSmall moleculenon-small cell lung carcinomaNEDD8 activating enzyme inhibitor2.0TerminatedClinicalTrials
PEVONEDISTATSmall moleculemyelodysplastic syndromeNEDD8 activating enzyme inhibitor2.0WithdrawnClinicalTrials
PEVONEDISTATSmall moleculeacute lymphoblastic leukemiaNEDD8 activating enzyme inhibitor1.0CompletedClinicalTrials
PEVONEDISTATSmall moleculecancerNEDD8 activating enzyme inhibitor1.0CompletedClinicalTrials
PEVONEDISTATSmall moleculeacute myeloid leukemiaNEDD8 activating enzyme inhibitor1.0CompletedClinicalTrials
PEVONEDISTATSmall moleculemesotheliomaNEDD8 activating enzyme inhibitor1.0Active, not recruitingClinicalTrials
PEVONEDISTATSmall moleculehepatocellular carcinomaNEDD8 activating enzyme inhibitor2.0SuspendedClinicalTrials
PEVONEDISTATSmall moleculemultiple myelomaNEDD8 activating enzyme inhibitor1.0Active, not recruitingClinicalTrials
PEVONEDISTATSmall moleculediffuse large B-cell lymphomaNEDD8 activating enzyme inhibitor1.0WithdrawnClinicalTrials
PEVONEDISTATSmall moleculemyelodysplastic syndromeNEDD8 activating enzyme inhibitor1.0Active, not recruitingClinicalTrials
PEVONEDISTATSmall moleculemyelodysplastic syndromeNEDD8 activating enzyme inhibitor2.0CompletedClinicalTrials